MPS IIIA: GSE97759

SummaryTissue/CellTreatment
OntologiesGenesBrain, BloodNo
OntologiesGenesBrainAAVrh74
OntologiesGenesBrainNo
OntologiesGenesBrainAAVrh74
OntologiesGenesBloodAAVrh74
OntologiesGenesBloodNo
OntologiesGenesBloodAAVrh74